Please confirm you are human
This browser or connection looks automated. Press and continuously hold the control for 3 seconds to enable Google-hosted web results and, when separately allowed, AI-assisted answers.
A successful check enables 100 search requests. Interactive access does not authorize scraping, systematic collection, or reuse of search output.
News
Clinical and zebrafish studies of truncating SF3B2- variants in craniofacial microsomia
7+ hour, 57+ min ago (14+ words) Springer Nature Link...
New Computational Tool Finds Hidden Asthma Genes Missed by Traditional Methods | Newswise
13+ hour, 20+ min ago (406+ words) Existing approaches like genome-wide association studies (GWAS) instead focus on genes that are often in the periphery of the gene regulatory network, however, and only indirectly affect disease. “All these existing tools assume that the actual disease genes are always…...
Galibra Neuroscience Receives FDA Orphan Drug and Rare Pediatric Disease Designations for SSADH Deficiency Gene Therapy
1+ week, 4+ day ago (279+ words) BOSTON, Aug. 5, 2026 /PRNewswire/ -- Galibra Neuroscience announced a significant regulatory milestone with the receipt of both Orphan Drug Designation (ODD) and Rare Pediatric Disease Designation (RPDD) from the U.S. Food and Drug Administration (FDA) for the company's investigational gene therapy for succinic…...
Multi-database study identifies cervical cancer targets tailored to tumor
14+ hour, 23+ min ago (667+ words) Cervical cancer may need more than a single therapeutic strategy, according to a new study that combines large-scale gene-expression analysis with laboratory testing to identify cell-surface proteins suitable for more precisely targeted antibody-drug conjugates. The work suggests that different cervical…...
CTPS1 Drives Lung Adenocarcinoma Progression, Revealing a Targetable
14+ hour, 57+ min ago (69+ words) A metabolic enzyme best known for helping cells build the genetic material needed for growth has emerged as a potential weakness in lung adenocarcinoma, the most common major subtype of lung cancer. In a study published in the British Journal…...
PTC Therapeutics Wins Auction For ST-920 Fabry Gene Therapy In Deal Worth Up To $211 Million
2+ day, 19+ hour ago (588+ words) PTC Therapeutics has been selected as the winning bidder to acquire Sangamo Therapeutics’ ST-920 Fabry disease gene therapy program in a bankruptcy auction for $111 million upfront and up to $100 million in additional regulatory milestone payments. The acquisition could have a…...
We Helped Create A $4 Million Gene Therapy For Our Son. Then We Had To Decide If We Should Give It To Him.
2+ day, 20+ hour ago (1171+ words) I was a side character in a typical Western, strutting around the saloon, dodging tumbleweeds and trouble. Suddenly, our neurosurgeon popped up behind the swinging doors, a huge grin on his chiseled face: "It's time for the surgery!" "We're not…...
In the US, genetic screening of embryos based on IQ and appearance is available
3+ day, 3+ hour ago (515+ words) The Herasight service may charge up to $50 thousand for the analysis of an unlimited number of embryos. Professional medical organisations consider polygenic selection to be insufficiently accurate for clinical practice. Briefly about the main points Nucleus advertises analysis of over…...
Body fat in pregnancy may influence child ADHD risk through inflammation
3+ day, 19+ hour ago (811+ words) By Eric W. Dolan, Adipose tissue, commonly known as body fat, actively produces and secretes various immune molecules called cytokines. When body fat levels increase, this chemical signaling tends to trigger a state of persistent, low-grade systemic inflammation that is proportionate…...
Capricor shares soar as potential FDA lifeline revives Duchenne drug hopes
3+ day, 17+ hour ago (346+ words) Aug 14 (Reuters) – Capricor Therapeutics shares surged 70% on Friday after the company said the U.S. health regulator is willing to review new data on its experimental Duchenne muscular dystrophy drug. The stock had crashed last month after an FDA advisory panel…...