News
Organoids: AI meets the end of animal testing
2+ hour, 53+ min ago (291+ words) Biopharma company MSD has taken considered bets on healthcare AI, from drug discovery platforms to diagnostics. Here's why the team's AI lead, David Rubin, sees tiny human tissue models as the next emerging area. The Global Health Innovation Fund had…...
AI-designed viral vectors achieve 50-fold brain enrichment over AAV9
3+ hour, 7+ min ago (537+ words) Preclinical findings from White Lab Genomics demonstrate that AI-designed viral vectors achieved approximately 50-fold higher brain DNA enrichment than AAV9 following intravenous injection in mice, while remaining undetectable in the liver." White Lab Genomics has announced new preclinical data showing that…...
Building a better model for drug delivery across the blood'brain barrier
8+ hour, 45+ min ago (822+ words) Getting drugs into the brain is notoriously difficult. The blood'brain barrier is extremely selective, blocking most large therapeutics from entering the brain. As a workaround, researchers have tried to exploit a protein called transferrin receptor 1, or Tf R1. Tf R1 is abundant…...
WVE: WVE-006 achieved up to 71% Z-AAT reduction and restored protective M-AAT levels in AATD
13+ hour, 46+ min ago (91+ words) Trading View WVE: WVE-006 achieved up to 71% Z-AAT reduction and restored protective M-AAT levels in AATD WVE-006, an RNA editing therapy for AATD, demonstrated robust safety and efficacy in the Restor AATion-2 study, with up to 71% reduction in mutant Z-AAT…...
JCR Pharmaceuticals Presents Preclinical Gene Therapy Data that Demonstrate Promising Central Nervous System Uptake at the American Society of Gene and Cell Therapy (ASGCT) 29th Annual Meeting
8+ hour, 3+ min ago (945+ words) Bio Space JCR Pharmaceuticals Presents Preclinical Gene Therapy Data that Demonstrate Promising Central Nervous System Uptake at the American Society of Gene and Cell Therapy (ASGCT) 29th Annual Meeting - Research Describes the Potential of JCR's Platform Technologies, Including JUST-AAV Gene Therapy,…...
Global Summit Proceedings Published in Frontiers Highlight Worldwide Innovation in Engineering and Medicine | Carle Illinois College of Medicine | Illinois
10+ hour, 48+ min ago (442+ words) The 2026 Global Consortium of Innovation and Engineering in Medicine (GCIEM) Global Summit proceedings have been published through'Frontiers Journals, documenting research and emerging technologies presented at the international conference held in Taipei, Taiwan. "Participants at the Global Summit came together in…...
JCR Pharmaceuticals Presents Preclinical Gene Therapy Data that Demonstrate Promising Central Nervou
16+ hour, 46+ min ago (1032+ words) - Research Describes the Potential of JCR's Platform Technologies, Including JUST-AAV Gene Therapy, to Facilitate Delivery of Therapies to the Central Nervous System -HYOGO, Japan--(BUSINESS WIRE)--JCR Pharmaceuticals Co. , Ltd. (TSE 4552; "JCR), a global specialty biopharmaceutical company dedicated to developing…...
DNA-guided CRISPR system targets RNA and expands Cas12 beyond gene editing
9+ hour, 50+ min ago (224+ words) A DNA-guided CRISPR platform could make RNA detection and control more stable, scalable, and precise, opening new routes for diagnostics, transcriptome engineering, and future therapeutic research. In the present study, researchers designed "DNA, a DNA-based guide that helps Cas12 systems find…...
Andelyn Biosciences unveils LVV Curator platform for cell therapy - Select Science news
13+ hour, 16+ min ago (606+ words) New platform leverages the established Curator platform methodology to industrialize Lentivirus processes from concept to clinic Andelyn Biosciences has launched the LVV Curator" Platform, a standardized lentiviral vector (LVV) manufacturing solution that applies the company's proven Curator" viral vector platform methodology…...
How scientist designed viruses that kill superbugs
1+ week, 4+ hour ago (735+ words) Scientists have sequenced samples from one in five South Australian cystic fibrosis patients as antibiotic resistance reaches crisis levels worldwide. Don't miss out on the headlines from Partner Content. Followed categories will be added to My News. From the smallest…...